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Adrenoleukodystrophy
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1	The company is located in the Parc TecnoCampus Mataró-Maresme ”la Caixa” leads a 1.6 million Euro round in Minoryx • Minoryx is dedicated to treating rare or orphan diseases, focusing on those derived from congen Add to Reading List Source URL: www.caixacapitalrisc.es Language: English - Date: 2015-01-23 06:13:25 Orphan drug Rare disease Adrenoleukodystrophy Caixabank Health Medicine La Caixa
2	Rare Disease DayJoin MassBio, VHL Alliance, member companies, patient groups, patients and legislators to recognize Rare Disease Day. Friday, February 28th 11 a.m. Add to Reading List Source URL: www.massbio.org Language: English - Date: 2014-03-12 17:41:27 Hermansky–Pudlak syndrome Adrenoleukodystrophy National Organization for Rare Disorders Patient advocacy Patient Health Rare diseases Rare Disease Day
3	PDF Document Add to Reading List Source URL: www.hrsa.gov Language: English Peroxisomal disorders Adrenal gland disorders Leukodystrophies Organelles Adrenoleukodystrophy Adrenomyeloneuropathy ABCD1 Newborn screening Zellweger syndrome Health Medicine Rare diseases
4	HK J Paediatr (new series) 2005;10:[removed]MCQs Instruction: 1. Please use pencil to shade the box for the correct answer (see loose leaf page). 2. Send back the answer sheet to the Hong Kong College of Paediatricians f Add to Reading List Source URL: www.fmshk.com.hk Language: English - Date: 2006-06-28 04:23:07 Seizure types Epileptic seizure Catamenial epilepsy Primidone Adrenoleukodystrophy Myoclonus Congenital heart defect Anticonvulsant Epilepsy Brain Central nervous system
5	JUNE[removed]NASDAQ: BLUE Transforming the Lives of Patients Add to Reading List Source URL: www.bluebirdbio.com Language: English - Date: 2014-12-05 11:30:09 Stem cells Biotechnology Emerging technologies Bioethics Gene therapy Thalassemia Beta-thalassemia Sickle-cell disease Adrenoleukodystrophy Medicine Health Biology
6	PROTOCOL ALD-102 AN OPEN LABEL, NON-RANDOMIZED, SINGLE DOSE, MULTI-CENTER PHASE 2/3 STUDY OF THE SAFETY AND EFFICACY OF LENTI-D MODIFIED AUTOLOGOUS STEM CELLS (LENTI-D DRUG PRODUCT) FOR THE TREATMENT OF SUBJECTS WITH CHI Add to Reading List Source URL: osp.od.nih.gov Language: English - Date: 2013-12-31 13:09:44 Peroxisomal disorders Rare diseases Adrenoleukodystrophy Leukodystrophies Hematopoietic stem cell transplantation Myelin Medicine Health Biology
7	INSIDE » Board Elects New Trustees » Martin Hetzer Receives Scholar Award » One on One with Bob Lizarraga Where cures begin. Add to Reading List Source URL: www.salk.edu Language: English - Date: 2012-04-12 21:07:44 Gene delivery Biotechnology Rare diseases Bioethics Gene therapy Viral vector Jesse Gelsinger Adrenoleukodystrophy Retrovirus Biology Health Molecular biology
8	X-linked Adrenoleukodystrophy (ALD) Fred Lorey, Ph.D Genetic Disease Screening Program, California Department of Public Health Add to Reading List Source URL: www.hrsa.gov Language: English - Date: 2014-12-04 01:13:43 Peroxisomal disorders Adrenal gland disorders Leukodystrophies Adrenoleukodystrophy Newborn screening Screening The Myelin Project Health Rare diseases Medicine
9	Paula K. Brazeal, President The United Leukodystrophy Foundation was founded in 1982 with a mission dedicated to helping children and adults who have leukodystrophy and assisting the family members, professionals, and s Add to Reading List Source URL: www.hrsa.gov Language: English - Date: 2014-12-04 01:12:59 Adrenoleukodystrophy Leukodystrophies Kennedy Krieger Institute Adrenomyeloneuropathy Hugo Moser Health Rare diseases Peroxisomal disorders
10	Secretary’s Advisory Committee on Heritable Disorders in Newborns and Children Summary of 28th Meeting September 13-14, 2012 Washington, DC Add to Reading List Source URL: www.hrsa.gov Language: English - Date: 2014-12-04 01:13:59 Epidemiology Newborn screening Pediatrics Kennedy Krieger Institute Hugo Moser March of Dimes Association of Public Health Laboratories Adrenoleukodystrophy Screening Health Medicine Rare diseases

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