Draft:SRP-4044

Results: 5



#Item
1Muscular dystrophy / Biology / Genetics / Mdx mouse / Clinical medicine / Duchenne muscular dystrophy / Dystrophin / Gene duplication / DMD / Draft:BMN 044 / Draft:SRP-4044

Research Review No. 97. Mice with Exon 2 Duplication. The Studies: The authors of this study note that around 11% of cases of Duchenne Muscular Dystrophy (DMD) are due to a duplication in the dystrophin gene (1). Of th

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Source URL: www.actionduchenne.org

Language: English - Date: 2015-12-16 04:42:02
2Muscular dystrophy / Clinical medicine / Duchenne muscular dystrophy / Medicine / Health / Mdx mouse / Dystrophin / Draft:BMN 044 / Draft:SRP-4044

Research Review NoNew techniques are racing ahead. The Studies: The studies to be discussed in this review confirm that working at the cutting edge as described in the previous Research Review (Nois procee

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Source URL: www.actionduchenne.org

Language: English - Date: 2016-05-03 09:17:05
3Muscular dystrophy / Drisapersen / Duchenne muscular dystrophy / Exon skipping / Draft:BMN 044 / Dystrophin / DMD / Draft:SRP-4044

Research Review No. 86. Recent exciting new Developments. A general oveview. Introduction:

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Source URL: www.actionduchenne.org

Language: English - Date: 2014-12-10 08:10:02
4Muscular dystrophy / Biotechnology / Duchenne muscular dystrophy / Sarepta Therapeutics / PTC Therapeutics / Exon skipping / Clinical trial / BioMarin Pharmaceutical / Draft:BMN 044 / Draft:SRP-4044

ROUNDTABLE SURVEY RESULTS Our pilot program in 2015 was very successful. We distributed and collected surveys from all 6 of our Roundtable events, which were held in Boston, MA, Pittsburgh, PA. Los Angeles, CA and Dubl

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Source URL: jettfoundation.org

Language: English - Date: 2016-01-26 12:45:27
5Action Duchenne Research Strategy Version)- Post national meeting 1

Action Duchenne Research Strategy Version)- Post national meeting 1

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Source URL: www.actionduchenne.org

Language: English - Date: 2014-04-17 10:21:48