1 ANN Newsletter - No. 5 / October 2011 C li ni ca l T r i al s: UPD ATE Exon Skipping

Source URL: www.ann.org.au

• Health
• Duchenne muscular dystrophy
• Dystrophin
• Fazio-Londe disease
• Limb-girdle muscular dystrophy
• Ataluren
• Brown-Vialetto-Van Laere syndrome
• Spinal muscular atrophy
• Congenital muscular dystrophy
• Muscular dystrophy
• Genetic genealogy
• Medical genetics

September 17, 2014 PTC Therapeutics Expands Global Presence in Support of Translarna™ Launch in Duchenne Muscular Dystrophy SOUTH PLAINFIELD, N.J., Sept. 17, 2014 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT)

Source URL: hbmpartners.com

• Genetics
• Genetic engineering
• Ataluren
• Duchenne muscular dystrophy
• PTC Therapeutics
• Nonsense mutation
• Dystrophin
• Cystic fibrosis
• Health
• Biology
• Muscular dystrophy

Phase 3 Study of Ataluren in Patients with Nonsense Mutation Duchenne Muscular Dystrophy: Frequently Asked Questions What is ataluren? Ataluren (formerly called PTC124®) is an investigational new drug, which means it is

Source URL: muscle.ca

• Pharmacology
• Research
• Bioethics
• Medical ethics
• Genetic engineering
• Ataluren
• Duchenne muscular dystrophy
• Placebo
• Medicine
• Clinical research
• Science

PTC Therapeutics Raises $26.6 Million In Private Placement Financing Company Developing Small-Molecule Drugs Targeting Post-Transcriptional Control Mechanisms Has Raised Over $130 Million To Date SOUTH PLAINFIELD, NJ - N

Source URL: capital.vulcan.com

• PTC Therapeutics
• Pharmacology
• Research
• Pharmaceutical sciences
• Ataluren
• Genetic engineering

Dr. Jack Parent, MD Dr. Lori Isom, PhD Dr. Miriam Meisler, PhD

Source URL: www.dravetfoundation.org

• Molecular genetics
• Protein biosynthesis
• Dravet Syndrome Foundation
• Mutation
• Nav1.1
• Stop codon
• Nonsense mutation
• Ataluren
• Sodium channel
• Biology
• Gene expression
• Ion channels

Microsoft PowerPoint - TsengCMDcopy

Source URL: www.curecmd.org

• Myostatin
• Dystrophin
• Congenital muscular dystrophy
• Creatine
• Skeletal striated muscle
• Ataluren
• Duchenne muscular dystrophy
• Muscular dystrophy
• Biology
• Health

COMMUNIQUE DE PRESSE Vendredi 23 mai 2014 AMM conditionnelle pour l’Ataluren Une première pour un médicament de thérapie innovante pour la myopathie de Duchenne

Source URL: www.myologie.org

COMMUNIQUE DE PRESSE Vendredi 23 mai 2014 AMM conditionnelle pour l’Ataluren Une première pour un médicament de thérapie innovante pour la myopathie de Duchenne

Source URL: www.institut-myologie.org