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Transposable element / Gene therapy / Transposase / Stem cell / Sleeping Beauty transposon system / Knockout rat / Biology / Mobile genetic elements / Molecular biology


Sleeping Beauty Mediated Transposition in Hematopoietic Stem Cells R. Scott McIvor, Ph.D. Chief Executive Officer, Chief Science Officer Discovery Genomics, Minneapolis MN
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Document Date: 2014-01-08 12:15:53


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Facility

Institute of Human Genetics Department / /

MedicalCondition

B Cell Leukemia / Junctional Epidermolysis Bullosa / Glioma / Hemophilia B / Hereditary Tyrosinemia / Hemophilia A / Human Disease / /

MedicalTreatment

Gene Therapy / /

Organization

Institute of Human Genetics Department of Genetics / Minneapolis MN Center for Genome Engineering Gene Therapy Program / University of Minnesota / /

Person

Gene Transf / Gene Ther / Discovery Genomics / /

Position

Chief Executive Officer / Chief Science Officer / /

Technology

Gene Therapy / Stem Cells / /

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