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Rare diseases / Drug discovery / Orphan drug / Pharmaceuticals policy / Morquio syndrome / Pharmaceutical industry / BioMarin Pharmaceutical / Mucopolysaccharidosis / National Organization for Rare Disorders / Health / Pharmaceutical sciences / Medicine


National Organization for Rare Disorders Remarks before the FDA Endocrinologic and Metabolic Drugs Advisory Committee Silver Spring, Maryland November 19, 2013 Good afternoon. My name is Diane Edquist Dorman, Vice Presid
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Document Date: 2013-11-22 12:36:21


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