Miglustat

Results: 17



#Item
11Lipid storage disorders / Rare diseases / Lipids / Miglustat / Piperidines / NPC1 / Curcumin / Sphingomyelin / Niemann–Pick disease / Biology / Chemistry / Biochemistry

NNPDF Grant #47 – Fran Platt TARGETING SPHINGOSINE STORAGE AS A NEW THERAPEUTIC APPROACH FOR NIEMANN-PICK TYPE C 6 month report

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Source URL: www.nnpdf.org

Language: English - Date: 2008-10-22 09:31:56
12Ketones / Miglustat / Piperidines / NPC1 / Ayub K. Ommaya / Clinical trial / Methadone / Medicine / Health / Chemistry

Microsoft Word - HPBCD Phase I Announcement

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Source URL: www.parseghian.org

Language: English - Date: 2012-12-03 11:38:17
13Niemann–Pick disease / NPC1 / Miglustat / Lysosomal storage disease / Medicine / Niemann-Pick disease /  type C / Lipid storage disorders / Rare diseases / Health

Niemann-Pick PERSEVERE To l l F r e e[removed][removed]

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Source URL: www.nnpdf.ca

Language: English
14Medicine / Niemann–Pick disease / Mathematical optimization / Complexity classes / Ara Parseghian / Actelion / Miglustat / NP-complete / Parseghian / Health / Lipid storage disorders / Rare diseases

SPRING[removed]A GOAL FOR LIFE For Friends and Supporters of the Ara Parseghian Medical Research Foundation

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Source URL: www.parseghian.org

Language: English - Date: 2009-08-07 14:59:43
15Rare diseases / Medicine / Niemann–Pick disease / Niemann-Pick disease /  type C / Cyclodextrin / Lysosomal storage disease / European Medicines Agency / Miglustat / Orphan drug / Health / Chemistry / Lipid storage disorders

PDF Document

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Source URL: www.ema.europa.eu

Language: English - Date: 2013-07-21 06:20:11
16Lipid storage disorders / Rare diseases / Pharmacology / Orphan drugs / Miglustat / Piperidines / Niemann–Pick disease / Actelion / Food and Drug Administration / Health / Medicine / Pharmaceutical sciences

PDF Document

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Source URL: www.fda.gov

Language: English
17Rare diseases / Biology / Glycolipids / Enzymes / Galactosides / Miglustat / Lysosomal storage disease / Globoside / Ganglioside / Chemistry / Lipid storage disorders / Health

PDF Document

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Source URL: glycob.oxfordjournals.org

Language: English
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