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![]() Date: 2013-07-21 06:20:11Rare diseases Medicine Niemann–Pick disease Niemann-Pick disease type C Cyclodextrin Lysosomal storage disease European Medicines Agency Miglustat Orphan drug Health Chemistry Lipid storage disorders | Source URL: www.ema.europa.euDownload Document from Source WebsiteFile Size: 125,21 KBShare Document on Facebook |