neurological disorders / several dozen neuromuscular disorders / catastrophic diseases / neuromuscular disease / human diseases / breast cancer / cancer / Spinal Muscular Atrophy / disease / genetic diseases / muscular dystrophies / deficiency / /
OperatingSystem
Isis / /
Organization
Federal Drug Administration / Columbia University / Harvard University / Muscular Dystrophy Association / MIT / Rosalind Franklin University in Chicago / SMA Foundation / /
Person
Mads Jensen / Phil Sharp / Michelle Hastings / Michael Zhang / Adrian Krainer Tinkering / Lou Gehrig / Luca Cartegni / Adrian Krainer / /
Position
full professor / postdoctoral researcher / technician / messenger / designer / Research Investigator / model for translational research / /